Gene therapies for pulmonary disease are close to final development
Gene therapy currently offers the only chance of curing genetic diseases such as cystic fibrosis and beta thalassaemia. Intensive research has been going on in this field for many years, however only a handful gene therapies are available at this point in time. Dr. Michael Kormann, junior professor at the Children’s Hospital at the University of Tübingen, and his team of researchers deal with genes that have the potential to cure disease; their work focuses on gene therapy techniques and on the correction of genes that lead to severe, hereditary lung diseases. They were able to prolong the life of mice suffering from surfactant protein B deficiency using modified ribonucleic acids.